One transgene, two myopathies: an MTM1 'cross gene therapy' for BIN1 deficiency?

Asgarian, Z; Siam, A; Counsell, JR

Counsell, JR (通讯作者),UCL Div Surg & Intervent Sci, Res Dept Targeted Intervent, Charles Bell House, London, England.

BRAIN, 2023; 146 (10): 3966