Next steps for the optimization of exon therapy for Duchenne muscular dystrophy

Filonova, G; Aartsma-Rus, A

Aartsma-Rus, A (通讯作者)，Leiden Univ, Med Ctr, Leiden, Netherlands.

EXPERT OPINION ON BIOLOGICAL THERAPY, 2023; 23 (2): 133

Abstract

IntroductionIt is established that the exon-skipping approach can restore dystrophin in Duchenne muscular dystrophy (DMD) patients. However, dystrophi......

Full Text Link


Links

期刊讨论 | 中国SCI论文 | 期刊主页 | 投稿经验 | 杂志官网 | 投稿链接 | 作者需知 | PMC链接 | Pubmed全文检索