Safety Concerns with Nusinersen, Risdiplam, and Onasemnogene Abeparvovec in Spinal Muscular Atrophy: A Real-World Pharmacovigilance Study

Zhuang, W; Lu, M; Wu, Y; Chen, ZH; Wang, MY; Wang, XD; Guan, SX; Lin, WL

Lin, WL (通讯作者),Xiamen Univ, Women & Childrens Hosp, Sch Med, Dept Pharm, 10 Zhenhai Rd, Xiamen, Peoples R China.

CLINICAL DRUG INVESTIGATION, 2023; ():