NEO1/NEO-EXT studies: Trends over time in exploratory efficacy of repeat avalglucosidase alfa dosing for up to 5.5 years in late-onset Pompe disease (LOPD) patients

Schoser, B; Barohn, RJ; Byrne, BJ; Goker-Alpan, O; Kishnani, PS; Ladha, S; Laforet, P; Mengel, KE; Pena, LDM; Sacconi, S; Straub, V; Trivedi, J; Van Damme, P; Van der Ploeg, AT; Vissing, J; Young, P; Haack, KA; Fleurinck, C; Johnson, J; Liu, K; Dimachkie, MM

EUROPEAN JOURNAL OF NEUROLOGY, 2020; 27 (): 486

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