Orphan Drugs In Development For The Treatment Of Friedreich's Ataxia: Focus On Omaveloxolone

Ghanekar, SD; Miller, WW; Meyer, CJ; Fenelon, KJ; Lacdao, A; Zesiewicz, TA

Zesiewicz, TA (reprint author), Univ S Florida, Dept Neurol, Ataxia Res Ctr, Tampa, FL 33620 USA.

DEGENERATIVE NEUROLOGICAL AND NEUROMUSCULAR DISEASE, 2019; 9 (): 103

Abstract

Friedreich's Ataxia (FRDA) is a devastating and progressive ataxia, marked by mitochondrial dysfunction and oxidative stress. Nrf2 activators such as ......

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