In vivo gene editing via homology-independent targeted integration for adrenoleukodystrophy treatment

Hong, SA; Seo, JH; Wi, S; Jung, ES; Yu, J; Hwang, GH; Yu, JH; Baek, A; Park, S; Bae, S; Cho, SR

Bae, S (通讯作者),Hanyang Univ, Dept Chem, Seoul 04673, South Korea.;Bae, S (通讯作者),Hanyang Univ, Res Inst Nat Sci, Seoul 04673, South Korea.;Cho, SR (通讯作者),Yonsei Univ, Coll Med, Dept & Res Inst Rehabil Med, 5th Floor,50-1 Yonsei Ro, Seoul 03722, South Korea.

MOLECULAR THERAPY, 2022; 30 (1): 119