Amplifying gene expression with RNA-targeted therapeutics

Khorkova, O; Stahl, J; Joji, A; Volmar, CH; Wahlestedt, C

Wahlestedt, C (通讯作者),Univ Miami, Ctr Therapeut Innovat, Miami, FL 33146 USA.;Wahlestedt, C (通讯作者),Univ Miami, Dept Psychiat & Behav Sci, Miami, FL 33146 USA.;Wahlestedt, C (通讯作者),Univ Miami, Dept Chem, Miami, FL 33146 USA.

NATURE REVIEWS DRUG DISCOVERY, 2023; 22 (7): 539

Abstract

Many diseases involve reduced or absent levels of a particular protein and would benefit from therapies that increase gene expression. In their Review......

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