Selecting Potent Guide RNAs with Minimal Off-Target Activity for the CRISPR/Cas9 Engineering of KSQ-001, An Engineered Tumor Infiltrating Lymphocyte (eTIL (TM))

Hohmann, AF; Gannon, H; Falla, A; Calnan, C; Sathitloetsakun, S; Hafeez, N; Grasberger, P; Brady, M; Kaberna, J; Tubo, N; Le Mercier, I; Keegan, S; Wrocklage, C; Bullock, C; Shenker, S; Franco, C; Cadzow, L; Stegmeier, F; Benson, MJ; Kryukov, GV; Schlabach, M

MOLECULAR THERAPY, 2020; 28 (4): 187