Restoring AADC enzyme synthesis in AADC deficiency: MRI-Guided Delivery of AAV2-hAADC Gene Therapy to the Midbrain

Bankiewicz, K; Pearson, T; Grijalvo-Perez, A; Viehoever, A; San Sebastian, W; Imamura-Ching, J; Seo, Y; Larson, P; Gupta, N

MOVEMENT DISORDERS, 2019; 34 (): S229