Optimization of Hydroxyacidoxidase 1(HAO1) Targeting ARCUS Nucleases for the Treatment of Primary Hyperoxaluria Type 1 (PH1)-MedSci.cn

Optimization of Hydroxyacidoxidase 1(HAO1) Targeting ARCUS Nucleases for the Treatment of Primary Hyperoxaluria Type 1 (PH1)

Owens, G; Lewis, WC; Jordan-Steele, M; Polak, R; Lape, J; Smith, J; Holt, J; Falls, G; Jantz, D

MOLECULAR THERAPY, 2022; 30 (4): 116