Clinical Perspective: Treating RPE65-Associated Retinal Dystrophy

Maguire, AM; Bennett, J; Aleman, EM; Leroy, BP; Aleman, TS

Aleman, TS (corresponding author), Univ Penn, Dept Ophthalmol, Perelman Sch Med, Ctr Adv Retinal & Ocular Therapeut, Philadelphia, PA 19104 USA.

MOLECULAR THERAPY, 2021; 29 (2): 442

Abstract

Until recently, there was no approved treatment for a retinal degenerative disease. Subretinal injection of a recombinant adeno-associated virus (AAV)......

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