Lumacaftor/Ivacaftor Treatment of Patients with Cystic Fibrosis Heterozygous for F508del-CFTR

Rowe, SM; McColley, SA; Rietschel, E; Li, XL; Bell, SC; Konstan, MW; Marigowda, G; Waltz, D; Boyle, MP

Rowe, SM (reprint author), Univ Alabama Birmingham, Div Pulm Allergy & Crit Care Med, MCLM 706,1918 Univ Blvd, Birmingham, AL 35294 USA.

ANNALS OF THE AMERICAN THORACIC SOCIETY, 2017; 14 (2): 213

Abstract

Rationale: In a prior study, lumacaftor/ivacaftor treatment (<= 28 d) in patients with cystic fibrosis (CF) heterozygous for F508del-CFTR did not i......

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