CRISPR Therapeutics for Duchenne Muscular Dystrophy

Erkut, E; Yokota, T

Yokota, T (通讯作者),Univ Alberta, Fac Med & Dent, Dept Med Genet, 8613-114 St, Edmonton, AB T6G 2H7, Canada.;Yokota, T (通讯作者),Friends Garrett Cumming Res & Muscular Dystrophy, 8613-114 St, Edmonton, AB T6G 2H7, Canada.

INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2022; 23 (3):

Abstract

Duchenne muscular dystrophy (DMD) is an X-linked recessive neuromuscular disorder with a prevalence of approximately 1 in 3500-5000 males. DMD manifes......

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