Stereopure Oligonucleotides for the Selective Silencing of Mutant Huntingtin

Dale, E; Frank-Kamenetsky, M; Taborn, K; Aklilu, K; Liu, YJ; Berkovitch, S; Brown, J; Kandasamy, P; Kumarasamy, J; Iwamoto, N; Yin, Y; Yang, HL; Standley, S; Favaloro, F; Longo, K; Byrne, M; Vargeese, C

NEUROTHERAPEUTICS, 2020; 17 (SUPPL 1): 26