Stereopure oligonucleotides achieve allele-selective reduction of P23H mutant rhodopsin

Vathipadiekal, V; Guo, LK; Yin, Y; Shen, Q; Yang, HL; Looby, R; Norwood, L; Fransen, J; Jalligampala, A; Noel, J; Vargeese, C; McCall, MA; Byrne, M

INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2020; 61 (7):