RNA editing with CRISPR-Cas13

Cox, DBT; Gootenberg, JS; Abudayyeh, OO; Franklin, B; Kellner, MJ; Joung, J; Zhang, F

Zhang, F (reprint author), Massachusetts Inst Technol MIT & Harvard, Broad Inst, Cambridge, MA 02142 USA.; Zhang, F (reprint author), MIT, McGovern Inst Brain Res, 77 Massachusetts Ave, Cambridge, MA 02139 USA.; Zhang, F (reprint author), MIT, Dept Brain

SCIENCE, 2017; 358 (6366): 1019

Abstract

Nucleic acid editing holds promise for treating genetic disease, particularly at the RNA level, where disease-relevant sequences can be rescued to yie......

Full Text Link