Genome-wide RNA-seq of iPSC-derived motor neurons indicates selective cytoskeletal perturbation in Brown-Vialetto disease that is partially rescued by riboflavin

Rizzo, F; Ramirez, A; Compagnucci, C; Salani, S; Melzi, V; Bordoni, A; Fortunato, F; Niceforo, A; Bresolin, N; Comi, GP; Bertini, E; Nizzardo, M; Corti, S

Corti, S (reprint author), Univ Milan, IRCCS Fdn Ca Granda Osped Maggiore Policlin, Dept Pathophysiol & Transplantat DEPT, Dino Ferrari Ctr,Neurosci Sect,Neurol Unit, Milan, Italy.

SCIENTIFIC REPORTS, 2017; 7 ( ):

Abstract

Riboflavin is essential in numerous cellular oxidation/reduction reactions but is not synthesized by mammalian cells. Riboflavin absorption occurs thr......

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