Clinical Development of Cell Therapies to Halt Lysosomal Storage Diseases: Results and Lessons Learned

Graceffa, V

Graceffa, V (通讯作者),Inst Technol Sligo, Cellular Hlth & Toxicol Res Grp CHAT, Ash Ln, Bellanode, Sligo, Ireland.;Graceffa, V (通讯作者),Inst Technol Sligo, Dept Life Sci, Ash Ln, Bellanode, Sligo, Ireland.

CURRENT GENE THERAPY, 2022; 22 (3): 191

Abstract

Although cross-correction was discovered more than 50 years ago, and held the promise of drastically improving disease management, still no cure exist......

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