AAV cis-regulatory sequences are correlated with ocular toxicity

Xiong, WJ; Wu, DM; Xue, YL; Wang, SK; Chung, MJ; Ji, XK; Rana, P; Zhao, SR; Mai, SY; Cepko, CL

Xiong, WJ (reprint author), City Univ Hong Kong, Dept Biomed Sci, Kowloon, Hong Kong, Peoples R China.; Xiong, WJ (reprint author), City Univ Hong Kong, Shenzhen Res Inst, Shenzhen 518057, Peoples R China.; Cepko, CL (reprint author), Harvard Med Sch, Dep

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2019; 116 (12): 5785