Tafamidis concentration required for transthyretin stabilisation in cerebrospinal fluid

Tsai, FJ; Jaeger, M; Coelho, T; Powers, ET; Kelly, JW

Powers, ET; Kelly, JW (通讯作者),Scripps Res Inst, Dept Chem, La Jolla, CA 92037 USA.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2023; 30 (3): 279

Abstract

BackgroundHereditary transthyretin (TTR) amyloidosis (ATTRv) initially presents as a polyneuropathy and/or a cardiomyopathy. Central nervous system (C......

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