Perspectives on Genetic Medicine for Cystic Fibrosis

Smirnikhina, SA

Smirnikhina, SA (通讯作者),Med Genet Res Ctr, Lab Genome Editing, Moskvorechye 1, Moscow 115522, Russia.

CURRENT GENE THERAPY, 2022; 22 (5): 386

Abstract

Like any inherited protein deficiency disease, cystic fibrosis (CF) is a good candidate for gene replacement therapy. Despite the tremendous efforts o......

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