Huntingtin Lowering Strategies

Marxreiter, F; Stemick, J; Kohl, Z

Marxreiter, F (corresponding author), Univ Hosp Erlangen, Dept Mol Neurol, Huntingtons Dis Outpatient Clin, Schwabachanlage 6, Erlangen 91054, Germany.; Marxreiter, F (corresponding author), Univ Hosp Erlangen, Dept Mol Neurol, Ctr Rare Movement Disorders, Schwabachanlage 6, Erlangen 91054, Germany.

INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2020; 21 (6):

Abstract

Trials using antisense oligonucleotide technology to lower Huntingtin levels in Huntington's disease (HD) are currently ongoing. This progress, taking......

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