Nusinersen as a Therapeutic Agent for Spinal Muscular Atrophy

Li, Q

Li, Q (corresponding author), ShiJiaZhuang Tradit Chinese Med Hosp, Dept Fus, 233 ZhongShan West Rd, Shijiazhuang 050051, Hebei, Peoples R China.

YONSEI MEDICAL JOURNAL, 2020; 61 (4): 273

Abstract

The reduction of survival motor neuron (SMN) protein causes spinal muscular atrophy (SMA), an autosomal recessive neuromuscular disease. Nusinersen is......

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