AAV-ie enables safe and efficient gene transfer to inner ear cells

Tan, FZ; Chu, CF; Qi, JY; Li, WY; You, D; Li, K; Chen, X; Zhao, WD; Cheng, C; Liu, XY; Qiao, YB; Su, B; He, SJ; Zhong, C; Li, HW; Chai, RJ; Zhong, GS

Tan, FZ; Zhong, GS (reprint author), ShanghaiTech Univ, iHuman Inst, Shanghai 201210, Peoples R China.; Zhong, GS (reprint author), ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China.; Chai, RJ (reprint author), Southeast Univ, MO

NATURE COMMUNICATIONS, 2019; 10 ():

Abstract

Hearing loss is the most common sensory disorder. While gene therapy has emerged as a promising treatment of inherited diseases like hearing loss, it ......

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