Allele-Selective Knockdown of MYH7 Using Antisense Oligonucleotides

Anderson, BR; Jensen, ML; Hagedorn, PH; Little, SC; Olson, RE; Ammar, R; Kienzle, B; Thompson, J; McDonald, I; Mercer, S; Vikesaa, J; Nordbo, B; Iben, L; Cao, Y; Natale, J; Dalton-Kay, G; Cacace, A; Hansen, BR; Hedtjarn, M; Koch, T; Bristow, LJ

MOLECULAR THERAPY-NUCLEIC ACIDS, 2020; 19 (): 1290